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Table of Contents: “…Introduction to Muscular Dystrophy -- 2.Muscular Dystrophy: Historical Background and Types -- 3.FSHD: The Most Common Type of MD? …”
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Subjects: “…Duchenne muscular dystrophy. http://id.loc.gov/authorities/subjects/sh86006749…”

Subjects: “…Muscular dystrophy Genetic aspects Congresses.…”

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Table of Contents: “…Risks in a Trial of an Innovative Treatment of Duchenne Muscular Dystrophy /…”
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Table of Contents: “…Animal Models for Inherited Muscle Diseases -- In Utero Muscle Gene Transfer -- Gene Therapy for the Respiratory Muscles -- Muscular Dystrophy Gene Therapy in Small Animal Models -- Antisense-Mediated Exon Skipping for Duchenne Muscular Dystrophy -- Systemic Treatment of Duchenne Muscular Dystrophy by Antisense Oligomer-Induced Exon Skipping -- RNAi Therapy for Dominant Muscular Dystrophies and Other Myopathies -- Combinatorial Gene Therapy Strategies for Treating Muscular Dystrophies -- Duchenne Cardiomyopathy Gene Therapy -- Systemic Gene Delivery for Muscle Gene Therapy -- Modulating Immune Responses in Muscle Gene Therapy -- Delivering Large Therapeutic Genes for Muscle Gene Therapy -- Muscle as a Metabolic Factory for Gene Therapy -- Muscle as a Target for Genetic Vaccine -- Combining Stem Cells and Exon Skipping Strategy to Treat Muscular Dystrophy -- Gene Therapy Clinical Trials for Muscular Dystrophies.…”
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Table of Contents: “…N-Glycan function revealed by gene inactivation -- Neural cell function -- Notch signaling and muscular dystrophy -- Glycolipid function -- Glycolipid interaction -- Galectin function -- Newly developed field.…”

Table of Contents: “…Pathology and Diagnosis of Muscular Dystrophies -- Standards of Care for Duchenne Muscular Dystrophy: Brief Treat-NMD Recommendations -- Genetics and Pathogenesis of Distal Muscular Dystrophies -- Phenotype Variations in Early Onset Pompe Disease: Diagnosis and Treatment Results with Myozyme® -- Diseases of the Human Mitochondrial Oxidative Phosphorylation System -- Mitochondrial Diseases: A Cross-Talk Between Mitochondrial and Nuclear Genomes -- Mitochondrial Disorders Due to Nuclear OXPHOS Gene Defects -- Coenzyme Q10 Deficiencies in Neuromuscular Diseases -- The Role of Mitochondrial Network Dynamics in the Pathogenesis of Charcot-Marie-Tooth Disease -- Pathogenesis and Treatment of Mitochondrial Disorders -- Biology of Peripheral Inherited Neuropathies: Schwann Cell Axonal Interactions -- Phenotype and Clinical Evolution of Charcot-Marie-Tooth Disease Type 1A Duplication -- Genotypes & Sensory Phenotypes in 2 New X-Linked Neuropathies (CMTX3 and dSMAX) and Dominant CMT/HMN Overlap Syndromes -- Natural History and Treatment of Peripheral Inherited Neuropathies -- Spinal Muscular Atrophy During Human Development: Where Are the Early Pathogenic Findings? …”
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Table of Contents: “…Annexinopathies -- Calpains and Human Disease -- Gelsolin and Diseases -- Guanylate Cyclase-Activating Proteins and Retina Disease -- Pathologies Involving the S100 Proteins and Rage -- The Calcium-Sensing Receptor: Physiology, Pathophysiology and Car-Based Therapeutics -- Physiological Roles Of The Ca2+/Cam-Dependent Protein kinase Cascade In Health and Disease -- Calcium Channelopathies: Voltage-Gated Calcium Channels -- Trp Channels In Disease -- Diseases associated with altered ryanodine receptor activity -- Inositol 1,4,5-tripshosphate receptor, calcium signalling and huntington’s disease -- Serca pumps and human diseases -- The plasma membrane calcium ATPase and disease -- Diseases involving the Golgi calcium pump -- Calcium signalling and cancer cell growth -- Calcium Misregulation and the Pathogenesis of Muscular Dystrophy -- Calcium and Cell Death -- Calcium and Cell Death: The Mitochondrial Connection -- Role of Calcium in the Pathogenesis of Alzheimer’s Disease and Transgenic Models -- Calcium and Cardiomyopathies -- Calcium Signalling and Calcium Transport in Bone Disease.…”
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Table of Contents: “…Molecular Considerations in Cell Transplant Imaging -- Considerations for Successful Encapsulated β Cell Therapy -- Stem Cell Therapy for Neurovascular and Traumatic Brain Diseases -- Cell Replacement Strategies for Parkinson's Disease -- Cell Therapy for Epilepsy -- Dendritic Cell-Based Cancer Therapies: Current Status and Future Directions -- Encapsulation Approaches to Cell Therapy -- Biomaterials and Cells for Re-Vascularization -- Cell Reprogramming for Cardiac Regeneration and Rare Disease Modeling -- Engineering Organoid Systems to Model Health and Disease -- 3D Printing for Cell Therapy Applications -- Cell Therapy for Ophthalmic Diseases -- Cell Therapy: Approaching a Partnership with Pharma -- Stem Cell Therapy in Duchenne Muscular Dystrophy.…”
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